%0 Journal Article
%T Strimvelis£¿ for Treating Severe Combined Immunodeficiency Caused by Adenosine Deaminase Deficiency: An Evidence Review Group Perspective of a NICE Highly Specialised Technology Evaluation
%A Edward Cox
%A Emily South
%A Nerys Woolacott
%A Nick Meader
%A Susan Griffin
%J Archive of "PharmacoEconomics Open".
%D 2019
%R 10.1007/s41669-018-0102-3
%X Schematic of the company¡¯s model structure. ADA-SCID adenosine deaminase deficiency¨Csevere combined immunodeficiency, GvHD graft versus host disease, HSCT haematopoietic stem cell transplant, IVIG intravenous Immunoglobulin, MRD matched related donor, MSD matched sibling donor, PEG-ADA polyethylene glycol-modified bovine adenosine deaminas
%U https://www.ncbi.nlm.nih.gov/pmc/articles/PMC6533345/