Strimvelis？ for Treating Severe Combined Immunodeficiency Caused by Adenosine Deaminase Deficiency: An Evidence Review Group Perspective of a NICE Highly Specialised Technology Evaluation

Schematic of the company’s model structure. ADA-SCID adenosine deaminase deficiency–severe combined immunodeficiency, GvHD graft versus host disease, HSCT haematopoietic stem cell transplant, IVIG intravenous Immunoglobulin, MRD matched related donor, MSD matched sibling donor, PEG-ADA polyethylene glycol-modified bovine adenosine deaminas